da Luca Bonadei | Ott 16, 2018 | Business
“https://www.biopharma-reporter.com”
da Luca Bonadei | Ott 16, 2018 | Business
“https://www.biopharma-reporter.com”
da Luca Bonadei | Ott 16, 2018 | Regulatory
“http://www.pmlive.com”
da Luca Bonadei | Ott 16, 2018 | Regolatorio
“http://www.pmlive.com”
da Super User | Ott 16, 2018 | NERVOUS SYSTEM DISORDERS - NEUROMUSCOLAR DISORDERS
Description Severe muscolar atrophy caused by motoneurons loss from the anterior horn of spinal cord Incidence SMA in Italy 8,5-10,3/100.000 new borns, ~23-27 patients SMA1 58%, ~14-15 patients ATMP Targeted population TBD SoC/therapies approved The only drug...